Biotechnologies for Gene Therapy

Biotechnologies for Gene Therapy portes grátis

Biotechnologies for Gene Therapy

RNA, CRISPR, Nanobots, and Preclinical Applications

Yun, Yang H.; Yoder, Kristine E.

Springer Nature Switzerland AG

06/2023

203

Mole

Inglês

9783030933357

15 a 20 dias

Descrição não disponível.
?1. Therapeutic potential of microRNAs and their nanoparticle-based delivery in the treatment of liver fibrosis.- 2. MicroRNA as a versatile regulator of Wnt signaling pathway in colorectal cancer.- 3. Small Activating RNA Therapy for Angiogenesis.- 4. Muscular dystrophy therapy using viral vector-based CRISPR/Cas.- 5. CRISPR-Cas based gene therapy to target viral infections.- 6. CRISPR targeting the integrated HTLV-1 virus.- 7. Retroviral vectors for gene therapy of monogenic diseases.- 8. DNA Origami Nanodevices for Therapeutic Delivery Applications.
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DNA nanobots;CRISPR gene therapy;microRNA gene therapy;DNA gene therapy;delivery microRNA;clinical applications RNA molecules;clinical applications DNA nanobots